Our focus

We are focusing on the development of treatments for neuromuscular diseases that currently lack treatment options, such as Duchenne muscular dystrophy (DMD).

We have dedicated more than a decade to researching potential treatments in our ongoing mission to make effective medicines available for these often overlooked, life-altering diseases. We are passionate about improving patients’ quality of life and our vision is to be a leader in providing treatments for rare diseases in these areas with high unmet medical needs.

Meet our Board of Directors

Meet our Executive Committee

Meet our Extended Management Team